{"id":233766,"date":"2023-01-27T09:03:28","date_gmt":"2023-01-27T08:03:28","guid":{"rendered":"https:\/\/fefac.cat\/empresarial\/?p=233766"},"modified":"2023-01-27T09:03:33","modified_gmt":"2023-01-27T08:03:33","slug":"pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos","status":"publish","type":"post","link":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/","title":{"rendered":"Pregunta de la setmana: quants medicaments orfes hi ha i per a quines malalties s&#8217;utilitzen?"},"content":{"rendered":"\n<h2 class=\"has-vivid-red-color has-text-color wp-block-heading\">Revisem les caracter\u00edstiques que ha de tenir un medicament per ser designat orfe<\/h2>\n\n\n\n<p>Un <strong>medicament orfe<\/strong> \u00e9s aquell producte destinat al <strong>tractament, la prevenci\u00f3 o el diagn\u00f2stic d\u2019una malaltia que posa en risc la vida o que \u00e9s molt greu, cr\u00f2nica i molt poc freq\u00fcent<\/strong>, i que, sense incentius per desenvolupar-lo, <strong>la seva venda a la Comunitat Europea dif\u00edcilment generaria el retorn suficient per justificar-ne la inversi\u00f3.<\/strong><\/p>\n\n\n\n<p>Des que la Comunitat Europea els va regular l\u2019any 2000 fins gener de 2021, <strong>s\u2019han autoritzat 197 medicaments orfes<\/strong>. Aquests han facilitat que pacients que fins al moment no disposaven de medicaments espec\u00edfics per a la seva malaltia veiessin ampliades les seves opcions de tractament. Aproximadament <strong>la meitat dels medicaments orfes autoritzats s\u00f3n medicaments contra el c\u00e0ncer i malalties immunit\u00e0ries.<\/strong> Els segueixen<strong> medicaments per a malalties del sistema digestiu i relacionades amb el metabolisme.<\/strong><\/p>\n\n\n\n<p><strong>Caracter\u00edstiques dels medicaments orfes<\/strong><\/p>\n\n\n\n<p>Perqu\u00e8 un medicament pugui optar a la designaci\u00f3 d&#8217;orfe ha de complir els requisits seg\u00fcents:<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li>el seu objectiu \u00e9s el diagn\u00f2stic, la <strong>prevenci\u00f3 o el tractament de malalties que amenacen la vida o que s\u00f3n cr\u00f2nicament debilitants<\/strong><\/li>\n\n\n\n<li>la malaltia<strong> afecta 5 persones o menys per cada 10.000 habitants a la UE<\/strong> o \u00e9s molt poc probable que, sense incentius, el medicament permeti recuperar la seva inversi\u00f3 en desenvolupament una vegada comercialitzat, i<\/li>\n\n\n\n<li><strong>la malaltia no disposa de\u00a0m\u00e8todes satisfactoris de diagn\u00f2stic, prevenci\u00f3 o tractament.<\/strong> En el cas que existeixin, el medicament suposa un benefici significatiu per a les persones afectades.<\/li>\n<\/ul>\n\n\n\n<p>Font d&#8217;informaci\u00f3: <strong><em><span style=\"text-decoration: underline\"><a href=\"https:\/\/medicaments.gencat.cat\/ca\/inici\/\" target=\"_blank\" rel=\"noreferrer noopener\">Medicaments.gencat.cat<\/a><\/span><\/em><\/strong><\/p>\n\n\n\n<p><\/p>\n\n\n\n<figure class=\"wp-block-embed is-type-wp-embed is-provider-fefac wp-block-embed-fefac\"><div class=\"wp-block-embed__wrapper\">\n<blockquote class=\"wp-embedded-content\" data-secret=\"jOvyjQN39f\"><a href=\"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-fefac-respon\/\">La FEFAC respon. Fes la teva pregunta!<\/a><\/blockquote><iframe class=\"wp-embedded-content lazyload\" sandbox=\"allow-scripts\" security=\"restricted\" style=\"position: absolute; clip: rect(1px, 1px, 1px, 1px);\" title=\"&#8220;La FEFAC respon. Fes la teva pregunta!&#8221; &#8212; FEFAC\" data-src=\"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-fefac-respon\/embed\/#?secret=DCuhrZwBLN#?secret=jOvyjQN39f\" data-secret=\"jOvyjQN39f\" width=\"600\" height=\"338\" frameborder=\"0\" marginwidth=\"0\" marginheight=\"0\" scrolling=\"no\" src=\"data:image\/svg+xml;base64,PHN2ZyB3aWR0aD0iMSIgaGVpZ2h0PSIxIiB4bWxucz0iaHR0cDovL3d3dy53My5vcmcvMjAwMC9zdmciPjwvc3ZnPg==\" data-load-mode=\"1\"><\/iframe>\n<\/div><\/figure>\n","protected":false},"excerpt":{"rendered":"<p>L&#8217;1 de gener de 2023 ha entrat en vigor l&#8217;impost sobre els envasos de pl\u00e0stic no reutilitzables, una nova normativa que afectar\u00e0 a totes aquelles empreses que duguin a terme operacions lligades a la fabricaci\u00f3, importaci\u00f3 o adquisici\u00f3 d&#8217;envasos de pl\u00e0stic no reutilitzables que vagin a utilitzar-se en el mercat espanyol.<\/p>\n","protected":false},"author":2313,"featured_media":17489,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_et_pb_use_builder":"","_et_pb_old_content":"","_et_gb_content_width":"","footnotes":""},"categories":[2066,2497,293,10,11,12,13,14,15,251],"tags":[1127,2495,2504],"class_list":["post-233766","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-categoria-actualitat","category-la-pregunta-de-la-setmana","category-gestio","category-empresarials","category-fefac","category-afb","category-afet","category-afell","category-agfe","category-reflexions-de-junta","tag-farmacia","tag-la-pregunta-de-la-setmana","tag-medicaments-orfes"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.5 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Pregunta de la setmana: quants medicaments orfes hi ha?<\/title>\n<meta name=\"description\" content=\"Pregunta de la setmana sobre el medicament orfe: quants medicaments orfes hi ha i per a quines malalties s&#039;utilitzen?\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/\" \/>\n<meta property=\"og:locale\" content=\"ca_ES\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Pregunta de la setmana: quants medicaments orfes hi ha?\" \/>\n<meta property=\"og:description\" content=\"Pregunta de la setmana sobre el medicament orfe: quants medicaments orfes hi ha i per a quines malalties s&#039;utilitzen?\" \/>\n<meta property=\"og:url\" content=\"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/\" \/>\n<meta property=\"og:site_name\" content=\"FEFAC\" \/>\n<meta property=\"article:published_time\" content=\"2023-01-27T08:03:28+00:00\" \/>\n<meta property=\"article:modified_time\" content=\"2023-01-27T08:03:33+00:00\" \/>\n<meta property=\"og:image\" content=\"https:\/\/fefac.cat\/empresarial\/wp-content\/uploads\/2020\/03\/painkillers-2525089_640.jpg\" \/>\n\t<meta property=\"og:image:width\" content=\"640\" \/>\n\t<meta property=\"og:image:height\" content=\"426\" \/>\n\t<meta property=\"og:image:type\" content=\"image\/jpeg\" \/>\n<meta name=\"author\" content=\"lclavijo@afb.cat\" \/>\n<meta name=\"twitter:card\" content=\"summary_large_image\" \/>\n<meta name=\"twitter:label1\" content=\"Escrit per\" \/>\n\t<meta name=\"twitter:data1\" content=\"lclavijo@afb.cat\" \/>\n\t<meta name=\"twitter:label2\" content=\"Temps estimat de lectura\" \/>\n\t<meta name=\"twitter:data2\" content=\"2 minuts\" \/>\n<script type=\"application\/ld+json\" class=\"yoast-schema-graph\">{\"@context\":\"https:\\\/\\\/schema.org\",\"@graph\":[{\"@type\":\"Article\",\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#article\",\"isPartOf\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/\"},\"author\":{\"name\":\"lclavijo@afb.cat\",\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/#\\\/schema\\\/person\\\/6ac15c94fb359972b6bfa9c752486744\"},\"headline\":\"Pregunta de la setmana: quants medicaments orfes hi ha i per a quines malalties s&#8217;utilitzen?\",\"datePublished\":\"2023-01-27T08:03:28+00:00\",\"dateModified\":\"2023-01-27T08:03:33+00:00\",\"mainEntityOfPage\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/\"},\"wordCount\":287,\"commentCount\":0,\"image\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#primaryimage\"},\"thumbnailUrl\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/wp-content\\\/uploads\\\/2020\\\/03\\\/painkillers-2525089_640.jpg\",\"keywords\":[\"farm\u00e0cia\",\"La pregunta de la setmana\",\"medicaments orfes\"],\"articleSection\":[\"Actualitat\",\"La pregunta de la setmana\",\"Gesti\u00f3\",\"Empresarials\",\"FEFAC\",\"AFB\",\"AFET\",\"AFELL\",\"AGFE\",\"Reflexions de Junta\"],\"inLanguage\":\"ca\",\"potentialAction\":[{\"@type\":\"CommentAction\",\"name\":\"Comment\",\"target\":[\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#respond\"]}]},{\"@type\":\"WebPage\",\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/\",\"url\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/\",\"name\":\"Pregunta de la setmana: quants medicaments orfes hi ha?\",\"isPartOf\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/#website\"},\"primaryImageOfPage\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#primaryimage\"},\"image\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#primaryimage\"},\"thumbnailUrl\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/wp-content\\\/uploads\\\/2020\\\/03\\\/painkillers-2525089_640.jpg\",\"datePublished\":\"2023-01-27T08:03:28+00:00\",\"dateModified\":\"2023-01-27T08:03:33+00:00\",\"author\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/#\\\/schema\\\/person\\\/6ac15c94fb359972b6bfa9c752486744\"},\"description\":\"Pregunta de la setmana sobre el medicament orfe: quants medicaments orfes hi ha i per a quines malalties s'utilitzen?\",\"breadcrumb\":{\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#breadcrumb\"},\"inLanguage\":\"ca\",\"potentialAction\":[{\"@type\":\"ReadAction\",\"target\":[\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/\"]}]},{\"@type\":\"ImageObject\",\"inLanguage\":\"ca\",\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#primaryimage\",\"url\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/wp-content\\\/uploads\\\/2020\\\/03\\\/painkillers-2525089_640.jpg\",\"contentUrl\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/wp-content\\\/uploads\\\/2020\\\/03\\\/painkillers-2525089_640.jpg\",\"width\":640,\"height\":426},{\"@type\":\"BreadcrumbList\",\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\\\/#breadcrumb\",\"itemListElement\":[{\"@type\":\"ListItem\",\"position\":1,\"name\":\"Home\",\"item\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/\"},{\"@type\":\"ListItem\",\"position\":2,\"name\":\"Pregunta de la setmana: quants medicaments orfes hi ha i per a quines malalties s&#8217;utilitzen?\"}]},{\"@type\":\"WebSite\",\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/#website\",\"url\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/\",\"name\":\"FEFAC\",\"description\":\"Federaci\u00f3 d&#039;Associacions de Farm\u00e0cies de Catalunya\",\"potentialAction\":[{\"@type\":\"SearchAction\",\"target\":{\"@type\":\"EntryPoint\",\"urlTemplate\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/?s={search_term_string}\"},\"query-input\":{\"@type\":\"PropertyValueSpecification\",\"valueRequired\":true,\"valueName\":\"search_term_string\"}}],\"inLanguage\":\"ca\"},{\"@type\":\"Person\",\"@id\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/#\\\/schema\\\/person\\\/6ac15c94fb359972b6bfa9c752486744\",\"name\":\"lclavijo@afb.cat\",\"url\":\"https:\\\/\\\/fefac.cat\\\/empresarial\\\/author\\\/laura-2\\\/\"}]}<\/script>\n<!-- \/ Yoast SEO plugin. -->","yoast_head_json":{"title":"Pregunta de la setmana: quants medicaments orfes hi ha?","description":"Pregunta de la setmana sobre el medicament orfe: quants medicaments orfes hi ha i per a quines malalties s'utilitzen?","robots":{"index":"index","follow":"follow","max-snippet":"max-snippet:-1","max-image-preview":"max-image-preview:large","max-video-preview":"max-video-preview:-1"},"canonical":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/","og_locale":"ca_ES","og_type":"article","og_title":"Pregunta de la setmana: quants medicaments orfes hi ha?","og_description":"Pregunta de la setmana sobre el medicament orfe: quants medicaments orfes hi ha i per a quines malalties s'utilitzen?","og_url":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/","og_site_name":"FEFAC","article_published_time":"2023-01-27T08:03:28+00:00","article_modified_time":"2023-01-27T08:03:33+00:00","og_image":[{"width":640,"height":426,"url":"https:\/\/fefac.cat\/empresarial\/wp-content\/uploads\/2020\/03\/painkillers-2525089_640.jpg","type":"image\/jpeg"}],"author":"lclavijo@afb.cat","twitter_card":"summary_large_image","twitter_misc":{"Escrit per":"lclavijo@afb.cat","Temps estimat de lectura":"2 minuts"},"schema":{"@context":"https:\/\/schema.org","@graph":[{"@type":"Article","@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#article","isPartOf":{"@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/"},"author":{"name":"lclavijo@afb.cat","@id":"https:\/\/fefac.cat\/empresarial\/#\/schema\/person\/6ac15c94fb359972b6bfa9c752486744"},"headline":"Pregunta de la setmana: quants medicaments orfes hi ha i per a quines malalties s&#8217;utilitzen?","datePublished":"2023-01-27T08:03:28+00:00","dateModified":"2023-01-27T08:03:33+00:00","mainEntityOfPage":{"@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/"},"wordCount":287,"commentCount":0,"image":{"@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#primaryimage"},"thumbnailUrl":"https:\/\/fefac.cat\/empresarial\/wp-content\/uploads\/2020\/03\/painkillers-2525089_640.jpg","keywords":["farm\u00e0cia","La pregunta de la setmana","medicaments orfes"],"articleSection":["Actualitat","La pregunta de la setmana","Gesti\u00f3","Empresarials","FEFAC","AFB","AFET","AFELL","AGFE","Reflexions de Junta"],"inLanguage":"ca","potentialAction":[{"@type":"CommentAction","name":"Comment","target":["https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#respond"]}]},{"@type":"WebPage","@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/","url":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/","name":"Pregunta de la setmana: quants medicaments orfes hi ha?","isPartOf":{"@id":"https:\/\/fefac.cat\/empresarial\/#website"},"primaryImageOfPage":{"@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#primaryimage"},"image":{"@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#primaryimage"},"thumbnailUrl":"https:\/\/fefac.cat\/empresarial\/wp-content\/uploads\/2020\/03\/painkillers-2525089_640.jpg","datePublished":"2023-01-27T08:03:28+00:00","dateModified":"2023-01-27T08:03:33+00:00","author":{"@id":"https:\/\/fefac.cat\/empresarial\/#\/schema\/person\/6ac15c94fb359972b6bfa9c752486744"},"description":"Pregunta de la setmana sobre el medicament orfe: quants medicaments orfes hi ha i per a quines malalties s'utilitzen?","breadcrumb":{"@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#breadcrumb"},"inLanguage":"ca","potentialAction":[{"@type":"ReadAction","target":["https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/"]}]},{"@type":"ImageObject","inLanguage":"ca","@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#primaryimage","url":"https:\/\/fefac.cat\/empresarial\/wp-content\/uploads\/2020\/03\/painkillers-2525089_640.jpg","contentUrl":"https:\/\/fefac.cat\/empresarial\/wp-content\/uploads\/2020\/03\/painkillers-2525089_640.jpg","width":640,"height":426},{"@type":"BreadcrumbList","@id":"https:\/\/fefac.cat\/empresarial\/pregunta-setmana-quants-medicament-orfes-hi-ha-malalties-usos\/#breadcrumb","itemListElement":[{"@type":"ListItem","position":1,"name":"Home","item":"https:\/\/fefac.cat\/empresarial\/"},{"@type":"ListItem","position":2,"name":"Pregunta de la setmana: quants medicaments orfes hi ha i per a quines malalties s&#8217;utilitzen?"}]},{"@type":"WebSite","@id":"https:\/\/fefac.cat\/empresarial\/#website","url":"https:\/\/fefac.cat\/empresarial\/","name":"FEFAC","description":"Federaci\u00f3 d&#039;Associacions de Farm\u00e0cies de Catalunya","potentialAction":[{"@type":"SearchAction","target":{"@type":"EntryPoint","urlTemplate":"https:\/\/fefac.cat\/empresarial\/?s={search_term_string}"},"query-input":{"@type":"PropertyValueSpecification","valueRequired":true,"valueName":"search_term_string"}}],"inLanguage":"ca"},{"@type":"Person","@id":"https:\/\/fefac.cat\/empresarial\/#\/schema\/person\/6ac15c94fb359972b6bfa9c752486744","name":"lclavijo@afb.cat","url":"https:\/\/fefac.cat\/empresarial\/author\/laura-2\/"}]}},"_links":{"self":[{"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/posts\/233766","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/users\/2313"}],"replies":[{"embeddable":true,"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/comments?post=233766"}],"version-history":[{"count":0,"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/posts\/233766\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/media\/17489"}],"wp:attachment":[{"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/media?parent=233766"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/categories?post=233766"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/fefac.cat\/empresarial\/wp-json\/wp\/v2\/tags?post=233766"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}