{"id":8875,"date":"2018-03-01T14:59:47","date_gmt":"2018-03-01T14:59:47","guid":{"rendered":"http:\/\/fefac.cat\/empresarial\/?p=8875"},"modified":"2018-03-01T14:59:47","modified_gmt":"2018-03-01T14:59:47","slug":"2-de-cada-5-nous-medicaments-sn-per-a-malalties-m","status":"publish","type":"post","link":"https:\/\/fefac.cat\/empresarial\/2-de-cada-5-nous-medicaments-sn-per-a-malalties-m\/","title":{"rendered":"2 de cada 5 nous medicaments s\u00f3n per a malalties minorit\u00e0ries"},"content":{"rendered":"<p>El 40% de tots els medicaments aprovats a Europa i els Estats Units que inclouen un nou principi actiu estan indicats per a l&#39;abordatge de patologies minorit&agrave;ries, segons informa la patronal dels laboratoris, Farmaindustria, amb motiu del Dia Mundial d&rsquo;aquestes malalties, celebrat el 28 de febrer.<\/p>\n<p>Les &uacute;ltimes dades procedents de les dues principals ag&egrave;ncies reguladores del m&oacute;n, l&#39;European Medicines Agency (EMA) i la Food and Drug Administration (FDA), dels Estats Units, corresponents a 2017, confirmen aquesta tend&egrave;ncia positiva. En el primer cas, el 40% dels 35 medicaments amb un nou principi actiu que van rebre opini&oacute; positiva de l&#39;EMA, &eacute;s a dir 14, s&oacute;n per al tractament de malalties poc freq&uuml;ents.<\/p>\n<p>L&rsquo;EMA destaca les aportacions terap&egrave;utiques dels nous f&agrave;rmacs orfes, entre els quals figuren medicaments contra patologies considerades rares com la queratitis neurotr&ograve;fica, el neuroblastoma o la s&iacute;ndrome carcinoide, entre d&#39;altres.<\/p>\n<p>Pel que fa als Estats Units, un total de 18 medicaments, que representen el 39% de les noves mol&egrave;cules aprovades per la FDA durant l&#39;any passat, s&oacute;n ter&agrave;pies dirigides a malalties poc freq&uuml;ents (que afecten a menys de 200.000 ciutadans en el conjunt dels Estats Units). Entre aquests nous medicaments, la FDA destaca un nou f&agrave;rmac per tractar una forma espec&iacute;fica de la malaltia de Batten i un altre dirigit a prevenir o reduir els episodis hemorr&agrave;gics en pacients amb un tipus concret d&#39;hemof&iacute;lia A.<\/p>\n<p>&ldquo;Aquests bons resultats en medicaments orfes no s&oacute;n aliens a les pol&iacute;tiques de protecci&oacute; de la propietat industrial aplicades a aquests f&agrave;rmacs, ja que han afavorit notablement la seva investigaci&oacute; i desenvolupament en benefici de tots&rdquo;, explica el director del Departament T&egrave;cnic de Farmaindustria, Emili Esteve.<\/p>\n<p>Segons la seva opini&oacute;, &quot;tot i que queda molt cam&iacute; per rec&oacute;rrer, les dades sobre els nous tractaments disponibles per a combatre les malalties poc freq&uuml;ents s&oacute;n esperan&ccedil;adors i demostren que si tots els agents implicats (ind&uacute;stria, administracions, professionals sanitaris, centres de recerca, hospitals, etc.) continuem treballant junts dins d&#39;un marc legal afavoridor d&rsquo;investigaci&oacute;, seguirem aconseguint bons resultats per als pacients en els propers anys&rdquo;.<\/p>\n","protected":false},"excerpt":{"rendered":"<p>El 40% de tots els medicaments aprovats a Europa i els Estats Units que inclouen un nou principi actiu estan indicats per a l&#39;abordatge de patologies minorit&agrave;ries, segons informa la [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_et_pb_use_builder":"","_et_pb_old_content":"","_et_gb_content_width":"","footnotes":""},"categories":[11,12,13,14,15,101],"tags":[180,233],"class_list":["post-8875","post","type-post","status-publish","format-standard","hentry","category-fefac","category-afb","category-afet","category-afell","category-agfe","category-sanitaria","tag-farmaindustria","tag-malalties-rares"],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.5 - 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